Project Scope

To evaluate the treatment landscape, unmet needs, and pricing/reimbursement potential for a hypothetical SMA product

Challenge

Our client, a leading innovator in developing therapies for spinal muscular atrophy, aimed to understand the expectations for the reimbursement and pricing of Product X for SMA, focusing on the maintenance year's price, while also gathering insights on the clinical trial design and its perceived clinical value

Solution

In-depth primary research was conducted to gather understanding on:

• SMA reimbursement landscape and unmet needs
• Perspectives on the pivotal clinical trial design, including its safety and efficacy evaluation across different patient populations
• Expectations for the pricing and reimbursement potential of Product X, focusing on the maintenance year and implications of specific price points

Results

• Successfully enabled our client to understand the current SMA landscape, perceptions on the clinical trial design, including strengths, weaknesses, across various SMA patient populations and comparisons with existing therapies. Alongside, the expectations regarding the product’s clinical value, maintenance year pricing, and reimbursement potential